Success Story

The first disease successfully treated by gene therapy was Severe Combined Immune Deficiency (SCID). Researchers at the National Institutes of Health used gene therapy to deliver functioning genes into the T-cells of a four-year-old girl. The girl's immune system functioning was boosted to 25% of normal. She has to continue receiving injections of the "repaired" T-cells, but lives an otherwise normal life. Thanks to this pioneering experiment, others who are afflicted with SCID can now receive treatment.

Explore More: Genetic Engineering
Copyright 2004, Iowa Public Television
The Explore More project is supported by funds from the
Roy J. Carver Charitable Trust
and the USDE Star Schools Program.